The Protalix/FDA denial for Gaucher drug

The FDA denied Protalix’s new Gaucher drug this past week.   I have received a number of emails from people asking me how this affects Hannah.

This has no affect on Hannah at all.  This drug is designed only for type 1 and would not even be an option for Hannah.

Unfortunately, no one is working on a drug for type 2 or type 3.

Comments

  1. Is there even “conversation” going on about a drug for type 2/3?