The FDA denied Protalix’s new Gaucher drug this past week. I have received a number of emails from people asking me how this affects Hannah.
This has no affect on Hannah at all. This drug is designed only for type 1 and would not even be an option for Hannah.
Unfortunately, no one is working on a drug for type 2 or type 3.
Is there even “conversation” going on about a drug for type 2/3?